An immune tolerance approach using transient low-dose methotrexate in the ERT-naïve setting of patients treated with a therapeutic protein: experience in infantile-onset Pompe disease

Zoheb B. Kazi, Ankit K. Desai, R. Bradley Troxler, David Kronn, Seymour Packman, Marta Sabbadini, William B Rizzo, Katalin Scherer, Omar Abdul-Rahman, Pranoot Tanpaiboon, Sheela Nampoothiri, Neerja Gupta, Annette Feigenbaum, Dmitriy M. Niyazov, Langston Sherry, Reeval Segel, Alison McVie-Wylie, Crystal Sung, Alexandra M. Joseph, Susan RichardsPriya S. Kishnani

Research output: Contribution to journal › Article › peer-review

9 Scopus citations

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