Exogenous Flupirtine as Potential Treatment for CLN3 Disease

Katia Maalouf, Joelle Makoukji, Sara Saab, Nadine J. Makhoul, Angelica V. Carmona, Nihar Kinarivala, Noël Ghanem, Paul C. Trippier, Rose Mary Boustany

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Chemical Compounds

Medicine & Life Sciences