X-linked spinal muscular atrophy in mice caused by autonomous loss of ATP7A in the motor neuron

Victoria L. Hodgkinson, Jeffery M. Dale, Michael L. Garcia, Gary A. Weisman, Jaekwon Lee, Jonathan D. Gitlin, Michael J. Petris

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Biochemistry, Genetics and Molecular Biology

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Pharmacology, Toxicology and Pharmaceutical Science

Neuroscience